Gene-based Therapeutics for Neurological Disorders: From Basic Science to Clinical Applications

This is a great opportunity to assemble a rich programme of international speakers to address the latest advances in gene therapy, from basic research of vector design, modelling and pre-clinical testing to clinical applications in CNS disorders such as Parkinson’s, Alzheimer’s, Huntington’s, motor neuron diseases and eye diseases.

The conference will bring together basic and clinical scientists to discuss recent discoveries in genetics and mechanisms of disease (e.g. the role of RNA metabolism and processing in neurological diseases, including amyotrophic lateral sclerosis (ALS), frontotemporal dementia (FTD), spinal muscular atrophy (SMA), and repeat expansion disorders) and how these discoveries could help develop novel gene based therapeutics for neurodegenerative diseases. Further topics such as challenges in vector manufacturing and views of regulatory agencies on gene therapy clinical applications will be discussed.

Organization: Fusion Conferences Ltd

(Gene-based Therapeutics for Neurological Disorders Conference's venue, via fusion-conferences.com)

Gene-based Therapeutics for Neurological Disorders: From Basic Science to Clinical Applications